Disease · MONDO_0016239
Trials11
Trials an Open Targets clinical report links to the disease, posted results first, then the largest. A trial is shown when the release's checks confirm its link to the disease and Drugs and targets shows its link to one of the disease's drugs.
1 to 11 of 11
Download this page as JSON| Trial | Title | Phase | Participants | Results first posted | Conditions | Drugs | Linked by | Source |
|---|---|---|---|---|---|---|---|---|
| NCT00001213 | Cysteamine Eye Drops to Treat Corneal Crystals in Cystinosis | Phase 2 | 328 | 2014-07-22 | Cystinosis | CYSTEAMINE | Its record names the disease | ClinicalTrials.gov |
| NCT01197378 | Long-Term Safety Follow-up Study of Cysteamine Bitartrate Delayed-release Capsules (RP103) | Phase 3 | 60 | 2018-07-24 | Cystinosis | CYSTEAMINE BITARTRATE | Its record names the disease | ClinicalTrials.gov |
| NCT01000961 | Phase 3 Study of Cysteamine Bitartrate Delayed-release (RP103) Compared to Cystagon® in Patients With Cystinosis | Phase 3 | 43 | 2014-11-19 | Cystinosis | CYSTEAMINE BITARTRATE | Its record names the disease | ClinicalTrials.gov |
| NCT01733316 | Open-Label, Safety and Superior Effectiveness Study of Cysteamine Bitartrate Delayed-Release Capsules (RP103) in Cystinosis | Phase 3 | 41 | 2017-05-24 | Cystinosis | CYSTEAMINE BITARTRATE | Its record names the disease | ClinicalTrials.gov |
| NCT01744782 | Safety/Effectiveness Study of Cysteamine Bitartrate Delayed-release Capsules (RP103) in Cysteamine Treatment Naive Patients With Cystinosis | Phase 3 | 17 | 2018-01-16 | Cystinosis | CYSTEAMINE BITARTRATE | Its record names the disease | ClinicalTrials.gov |
| NCT00872729 | Pilot Study of Safety, Tolerability, Pharmacokinetics/Pharmacodynamics of RP103 Compared to Cystagon® in Patients With Cystinosis | Phase 1/2 | 9 | 2014-10-28 | Cystinosis | CYSTEAMINE BITARTRATE | Its record names the disease | ClinicalTrials.gov |
| NCT00359684 | Use of Cysteamine in the Treatment of Cystinosis | 330 | Cystinosis | CYSTEAMINE | Its record names the disease | ClinicalTrials.gov | ||
| NCT00001736 | New Cysteamine Eye Drops Formulation to Treat Corneal Crystals in Cystinosis | Phase 1 | 51 | Cystinosis | CYSTEAMINE | Its record names the disease | ClinicalTrials.gov | |
| NCT05994534 | PK and PD Study of NPI-001 and Cysteamine Bitartrate | Phase 1/2 | 8 | Cystinosis | CYSTEAMINE BITARTRATE | Its record names the disease | ClinicalTrials.gov | |
| NCT04125927 | Cystadrops in Pediatric Cystinosis Patients From Six Months to Less Than Two Years Old (SCOB2) | Phase 3 | 5 | Cystinosis | CYSTEAMINE | Its record names the disease | ClinicalTrials.gov | |
| NCT02124070 | Therapeutic Effect of Recombinant Human Growth Hormone (rhGH) on the Myopathy of Cystinosis | Phase 1/2 | 0 | Cystinosis, Myopathy | SOMATROPIN | Its record names the disease | ClinicalTrials.gov |
diseases-2026-09-18-0.1.0
Sources 6
- ClinicalTrials.gov's posted results, through CTTI's AACTFreely available. Acknowledgement requested
- ChEMBL, through Open TargetsCC BY-SA 3.0
- ClinicalTrials.govNo license stated
- NLM's MeSHNLM's terms
- Open TargetsCC0 1.0
- PubMedNLM's terms
Each source's terms
- ClinicalTrials.gov's posted results, through CTTI's AACTClinicalTrials.gov data via Aggregate Analysis of ClinicalTrials.gov (AACT), CTTI. CTTI makes its materials freely available and requests acknowledgement. https://aact.ctti-clinicaltrials.org/documentation/299
- ChEMBL, through Open TargetsCC BY-SA 3.0, for the parts from ChEMBL. Read on 8 Nov 2026 at https://platform-docs.opentargets.org/licence
- ClinicalTrials.govnone stated
- NLM's MeSHNLM's
- Open TargetsCC0 1.0. Open Targets asks that users cite its latest paper: Buniello et al. 2025, Open Targets Platform: facilitating therapeutic hypotheses building in drug discovery, Nucleic Acids Research 53(D1):D1467, PMID 39657122. Read on 8 Nov 2026 at https://platform-docs.opentargets.org/licence
- PubMedNLM's terms
ClinicalTrials.gov's data carry an international copyright outside the United States: https://clinicaltrials.gov/about-site/terms-conditions.
For software
Read this list from software.
Twenty rows a page, as JSON. No key.
GET https://conductscience.org/api/diseases/v1/MONDO_0016239/trials