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Trial · NCT02908685

Participant flow210

How many started, completed or left each group, period by period.

PeriodMilestoneGroupParticipantsUnits counted
Part 1 Placebo-ControlledSTARTEDPart 1 Group A Cohort 1: Adolescents and Adults (3 mg Risdiplam)7
Part 1 Placebo-ControlledSTARTEDPart 1 Group A Cohort 2: Adolescents and Adults (5 mg Risdiplam)7
Part 1 Placebo-ControlledSTARTEDPart 1 Group A Cohort 1: Adolescents and Adults (Placebo)3
Part 1 Placebo-ControlledSTARTEDPart 1 Group A Cohort 2: Adolescents and Adults (Placebo)3
Part 1 Placebo-ControlledSTARTEDPart 1 Group B Cohort 1: Children (0.02 mg/kg Risdiplam)7
Part 1 Placebo-ControlledSTARTEDPart 1 Group B Cohort 2: Children (0.05 mg/kg Risdiplam)7
Part 1 Placebo-ControlledSTARTEDPart 1 Group B Cohort 3: Children (0.25 mg/kg Risdiplam)7
Part 1 Placebo-ControlledSTARTEDPart 1 Group B Cohort 1: Children (Placebo)3
Part 1 Placebo-ControlledSTARTEDPart 1 Group B Cohort 2: Children (Placebo)4
Part 1 Placebo-ControlledSTARTEDPart 1 Group B Cohort 3: Children (Placebo)3
Part 1 Placebo-ControlledSTARTEDPart 1 Group A: OLE0
Part 1 Placebo-ControlledSTARTEDPart 1 Group B: OLE0
Part 1 Placebo-ControlledSTARTEDPart 2: Risdiplam0
Part 1 Placebo-ControlledSTARTEDPart 2: Placebo0
Part 1 Placebo-ControlledCOMPLETEDPart 1 Group A Cohort 1: Adolescents and Adults (3 mg Risdiplam)7
Part 1 Placebo-ControlledCOMPLETEDPart 1 Group A Cohort 2: Adolescents and Adults (5 mg Risdiplam)7
Part 1 Placebo-ControlledCOMPLETEDPart 1 Group A Cohort 1: Adolescents and Adults (Placebo)3
Part 1 Placebo-ControlledCOMPLETEDPart 1 Group A Cohort 2: Adolescents and Adults (Placebo)3
Part 1 Placebo-ControlledCOMPLETEDPart 1 Group B Cohort 1: Children (0.02 mg/kg Risdiplam)7
Part 1 Placebo-ControlledCOMPLETEDPart 1 Group B Cohort 2: Children (0.05 mg/kg Risdiplam)7

Source ClinicalTrials.govtrials-2026-11-12-0.5.0

Sources 3

  • ClinicalTrials.gov's posted results, through CTTI's AACTFreely available. Acknowledgement requested
  • ClinicalTrials.govNo license stated
  • NIH RePORTER's clinical studies and project filesPublic domain
Each source's terms
  • ClinicalTrials.gov's posted results, through CTTI's AACTClinicalTrials.gov data via Aggregate Analysis of ClinicalTrials.gov (AACT), CTTI. CTTI makes its materials freely available and requests acknowledgement. https://aact.ctti-clinicaltrials.org/documentation/299
  • ClinicalTrials.govnone stated
  • NIH RePORTER's clinical studies and project filesPublic domain (NIH RePORTER)

ClinicalTrials.gov's data carry an international copyright outside the United States: https://clinicaltrials.gov/about-site/terms-conditions.

For software

Read this list from software.

Twenty rows a page, as JSON. No key.

GET https://conductscience.org/api/trials/v1/NCT02908685/flow