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Trial · NCT04089566

Participant flow18

How many started, completed or left each group, period by period.

PeriodMilestoneGroupParticipantsUnits counted
Overall StudySTARTEDPart A: 28/28 Milligrams (mg) Nusinersen6
Overall StudySTARTEDPart B: Infantile-Onset SMA: 12/12 mg Nusinersen25
Overall StudySTARTEDPart B: Infantile-Onset SMA: 50/28 mg Nusinersen50
Overall StudySTARTEDPart B: Later-Onset SMA: 12/12 mg Nusinersen8
Overall StudySTARTEDPart B: Later-Onset SMA: 50/28 mg Nusinersen16
Overall StudySTARTEDPart C: 50/28 mg Nusinersen40
Overall StudyCOMPLETEDPart A: 28/28 Milligrams (mg) Nusinersen6
Overall StudyCOMPLETEDPart B: Infantile-Onset SMA: 12/12 mg Nusinersen13
Overall StudyCOMPLETEDPart B: Infantile-Onset SMA: 50/28 mg Nusinersen35
Overall StudyCOMPLETEDPart B: Later-Onset SMA: 12/12 mg Nusinersen7
Overall StudyCOMPLETEDPart B: Later-Onset SMA: 50/28 mg Nusinersen16
Overall StudyCOMPLETEDPart C: 50/28 mg Nusinersen40
Overall StudyNOT COMPLETEDPart A: 28/28 Milligrams (mg) Nusinersen0
Overall StudyNOT COMPLETEDPart B: Infantile-Onset SMA: 12/12 mg Nusinersen12
Overall StudyNOT COMPLETEDPart B: Infantile-Onset SMA: 50/28 mg Nusinersen15
Overall StudyNOT COMPLETEDPart B: Later-Onset SMA: 12/12 mg Nusinersen1
Overall StudyNOT COMPLETEDPart B: Later-Onset SMA: 50/28 mg Nusinersen0
Overall StudyNOT COMPLETEDPart C: 50/28 mg Nusinersen0

Source ClinicalTrials.govtrials-2026-11-12-0.5.0

Sources 3

  • ClinicalTrials.gov's posted results, through CTTI's AACTFreely available. Acknowledgement requested
  • ClinicalTrials.govNo license stated
  • NIH RePORTER's clinical studies and project filesPublic domain
Each source's terms
  • ClinicalTrials.gov's posted results, through CTTI's AACTClinicalTrials.gov data via Aggregate Analysis of ClinicalTrials.gov (AACT), CTTI. CTTI makes its materials freely available and requests acknowledgement. https://aact.ctti-clinicaltrials.org/documentation/299
  • ClinicalTrials.govnone stated
  • NIH RePORTER's clinical studies and project filesPublic domain (NIH RePORTER)

ClinicalTrials.gov's data carry an international copyright outside the United States: https://clinicaltrials.gov/about-site/terms-conditions.

For software

Read this list from software.

Twenty rows a page, as JSON. No key.

GET https://conductscience.org/api/trials/v1/NCT04089566/flow