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Trial · NCT04221451

Results by group96

Each measurement the trial posted, group by group, in the words and numbers it posted.

OutcomeGroupCategoryValueSpreadUnits
PAP: PP: Percent Change From Baseline in CSF GM2 Biomarker to Week 104PAP: PP: Placebo-11.33Standard Error 4.23percent change
PAP: PP: Percent Change From Baseline in CSF GM2 Biomarker to Week 104PAP: PP: Venglustat-47.57Standard Error 3.04percent change
PAP: PP: Annualized Rate of Change From Baseline in the 9-HPT to Week 104PAP: PP: Placebo0.95Standard Error 1.92percent per year
PAP: PP: Annualized Rate of Change From Baseline in the 9-HPT to Week 104PAP: PP: Venglustat2.49Standard Error 1.35percent per year
PAP: SP: Percent Change From Baseline in Plasma and CSF Biomarkers (Glucosylceramide [GL-1] and GM2) to Week 104 in Juvenile/Adolescent Late-onset GM2 Gangliosidosis ParticipantsPAP: SP: VenglustatGL-1: CSF-82.35Standard Deviation 9.94percent change
PAP: SP: Percent Change From Baseline in Plasma and CSF Biomarkers (Glucosylceramide [GL-1] and GM2) to Week 104 in Juvenile/Adolescent Late-onset GM2 Gangliosidosis ParticipantsPAP: SP: VenglustatGL-1: Plasma-79.28Standard Deviation 2.56percent change
PAP: SP: Percent Change From Baseline in Plasma and CSF Biomarkers (Glucosylceramide [GL-1] and GM2) to Week 104 in Juvenile/Adolescent Late-onset GM2 Gangliosidosis ParticipantsPAP: SP: VenglustatGM2: CSF-43.41Standard Deviation 23.14percent change
PAP: SP: Percent Change From Baseline in Plasma and CSF Biomarkers (Glucosylceramide [GL-1] and GM2) to Week 104 in Juvenile/Adolescent Late-onset GM2 Gangliosidosis ParticipantsPAP: SP: VenglustatGM2: Plasma-55.91Standard Deviation 11.76percent change
PAP: SP: Percent Change From Baseline in Plasma and CSF GL-1 and GM1 Biomarkers to Week 104 in GM1 Gangliosidosis ParticipantsPAP: SP: VenglustatGL-1: CSF17.42Standard Deviation 188.41percent change
PAP: SP: Percent Change From Baseline in Plasma and CSF GL-1 and GM1 Biomarkers to Week 104 in GM1 Gangliosidosis ParticipantsPAP: SP: VenglustatGL-1: Plasma-80.42Standard Deviation 8.17percent change
PAP: SP: Percent Change From Baseline in Plasma and CSF GL-1 and GM1 Biomarkers to Week 104 in GM1 Gangliosidosis ParticipantsPAP: SP: VenglustatGM1: CSF-32.35Standard Deviation 17.46percent change
PAP: SP: Percent Change From Baseline in Plasma and CSF GL-1 and GM1 Biomarkers to Week 104 in GM1 Gangliosidosis ParticipantsPAP: SP: VenglustatGM1: Plasma-52.32Standard Deviation 16.76percent change
PAP: SP: Percent Change From Baseline in Plasma and CSF GL-1, GM2 and Monosialodihexosylganglioside (GM3) Biomarkers to Week 104 in Sialidosis Type 1 ParticipantPAP: SP: VenglustatGL-1: CSFNApercent change
PAP: SP: Percent Change From Baseline in Plasma and CSF GL-1, GM2 and Monosialodihexosylganglioside (GM3) Biomarkers to Week 104 in Sialidosis Type 1 ParticipantPAP: SP: VenglustatGL-1: PlasmaNApercent change
PAP: SP: Percent Change From Baseline in Plasma and CSF GL-1, GM2 and Monosialodihexosylganglioside (GM3) Biomarkers to Week 104 in Sialidosis Type 1 ParticipantPAP: SP: VenglustatGM2: CSFNApercent change
PAP: SP: Percent Change From Baseline in Plasma and CSF GL-1, GM2 and Monosialodihexosylganglioside (GM3) Biomarkers to Week 104 in Sialidosis Type 1 ParticipantPAP: SP: VenglustatGM2: PlasmaNApercent change
PAP: SP: Percent Change From Baseline in Plasma and CSF GL-1, GM2 and Monosialodihexosylganglioside (GM3) Biomarkers to Week 104 in Sialidosis Type 1 ParticipantPAP: SP: VenglustatGM3: CSFNApercent change
PAP: SP: Percent Change From Baseline in Plasma and CSF GL-1, GM2 and Monosialodihexosylganglioside (GM3) Biomarkers to Week 104 in Sialidosis Type 1 ParticipantPAP: SP: VenglustatGM3: PlasmaNApercent change
PAP: SP: Percent Change From Baseline in Plasma and CSF GL-1, GM1 and GM3 Biomarkers to Week 104 in Juvenile/Adult Galactosialidosis ParticipantsPAP: SP: VenglustatGL-1: CSFNApercent change
PAP: SP: Percent Change From Baseline in Plasma and CSF GL-1, GM1 and GM3 Biomarkers to Week 104 in Juvenile/Adult Galactosialidosis ParticipantsPAP: SP: VenglustatGL-1: PlasmaNApercent change

Source ClinicalTrials.govtrials-2026-11-12-0.5.0

Sources 3

  • ClinicalTrials.gov's posted results, through CTTI's AACTFreely available. Acknowledgement requested
  • ClinicalTrials.govNo license stated
  • NIH RePORTER's clinical studies and project filesPublic domain
Each source's terms
  • ClinicalTrials.gov's posted results, through CTTI's AACTClinicalTrials.gov data via Aggregate Analysis of ClinicalTrials.gov (AACT), CTTI. CTTI makes its materials freely available and requests acknowledgement. https://aact.ctti-clinicaltrials.org/documentation/299
  • ClinicalTrials.govnone stated
  • NIH RePORTER's clinical studies and project filesPublic domain (NIH RePORTER)

ClinicalTrials.gov's data carry an international copyright outside the United States: https://clinicaltrials.gov/about-site/terms-conditions.

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GET https://conductscience.org/api/trials/v1/NCT04221451/results