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Trial · NCT07887828

Registered outcomes17

Each outcome the trial registered, primary first, in ClinicalTrials.gov's words.

ListOutcomeTime frameDescription
PrimaryChange From Baseline in Modified Friedreich's Ataxia Rating Scale (mFARS) ScoreBaseline up to approximately 24 months
PrimaryChange From Baseline in Activities of Daily Living (ADL) ScoreBaseline up to approximately 24 months
PrimaryClinical History: Age of OnsetAt Baseline
PrimaryClinical History: Family HistoryAt Baseline
PrimaryClinical History: MedicationAt Baseline
PrimaryClinical History: TreatmentAt Baseline
PrimaryDiagnostic Information: Age at DiagnosisAt Baseline
PrimaryDiagnostic Information: Proportion of Participants With Frataxin (FXN) MutationsAt Baseline
SecondaryEstimation of Frequency of Friedreich's Ataxia (FRDA)Up to approximately 24 months
SecondaryBaseline Demographics: AgeAt Baseline
SecondaryBaseline Demographics: SexAt Baseline
SecondaryBaseline Demographics: GeographyAt Baseline
SecondaryBaseline Demographics: Race/EthnicityAt Baseline
SecondaryBaseline Demographics: HeightAt Baseline
SecondaryBaseline Demographics: WeightAt Baseline
SecondaryNumber of Participants With Associated ComorbiditiesUp to approximately 24 months
SecondaryNumber of Participants With Clinical History of FRDAUp to approximately 24 months

Source ClinicalTrials.govtrials-2026-11-12-0.5.0

Sources 3

  • ClinicalTrials.gov's posted results, through CTTI's AACTFreely available. Acknowledgement requested
  • ClinicalTrials.govNo license stated
  • NIH RePORTER's clinical studies and project filesPublic domain
Each source's terms
  • ClinicalTrials.gov's posted results, through CTTI's AACTClinicalTrials.gov data via Aggregate Analysis of ClinicalTrials.gov (AACT), CTTI. CTTI makes its materials freely available and requests acknowledgement. https://aact.ctti-clinicaltrials.org/documentation/299
  • ClinicalTrials.govnone stated
  • NIH RePORTER's clinical studies and project filesPublic domain (NIH RePORTER)

ClinicalTrials.gov's data carry an international copyright outside the United States: https://clinicaltrials.gov/about-site/terms-conditions.

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