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Disease · MONDO_0009290

Comparisons in its trials20

Comparisons Trial comparisons calculated in the trials shown here, most participants first. A comparison in one of these trials does not always compare a treatment for the disease, so read the two groups.

ComparisonGroup 1, with the outcomeGroup 2, with the outcomeParticipantsTrialSource
Cipaglucosidase Alfa/Miglustat vs Alglucosidase Alfa/Placebo: deaths from any cause0 of 850 of 38123NCT03729362Trial comparisons
Cipaglucosidase Alfa/Miglustat vs Alglucosidase Alfa/Placebo: serious adverse events8 of 851 of 38123NCT03729362Trial comparisons
Cipaglucosidase Alfa/Miglustat vs Alglucosidase Alfa/Placebo: Number of Participants Improving on Both 6MWD and % Predicted FVC at Week 5214 of 850 of 37122NCT03729362Trial comparisons
Treatment Continued Group vs Treatment Switched Group: deaths from any cause1 of 810 of 37118NCT04138277Trial comparisons
Treatment Continued Group vs Treatment Switched Group: serious adverse events17 of 8110 of 37118NCT04138277Trial comparisons
Alglucosidase Alfa: <18 Years vs Alglucosidase Alfa: >=18 Years: deaths from any cause0 of 100 of 1020NCT01410890Trial comparisons
Alglucosidase Alfa: <18 Years vs Alglucosidase Alfa: >=18 Years: serious adverse events1 of 100 of 1020NCT01410890Trial comparisons
Albuterol vs Placebo Comparator: Number of Participants With Adverse Events.5 of 85 of 513NCT01885936Trial comparisons
Albuterol vs Placebo Comparator: deaths from any cause0 of 80 of 513NCT01885936Trial comparisons
Albuterol vs Placebo Comparator: serious adverse events0 of 80 of 513NCT01885936Trial comparisons
Clenbuterol vs Placebo Comparator: deaths from any cause0 of 80 of 513NCT01942590Trial comparisons
Clenbuterol vs Placebo Comparator: Number of Participants With a Change in Aspartate Aminotransferase (AST), Alanine Transaminase (ALT), and Bilirubin Representing Liver Toxicity0 of 80 of 513NCT01942590Trial comparisons
Clenbuterol vs Placebo Comparator: Number of Participants With a Change in Creatine Kinase (CK) Reflecting Worsening of Muscle Involvement1 of 80 of 513NCT01942590Trial comparisons
Clenbuterol vs Placebo Comparator: serious adverse events1 of 80 of 513NCT01942590Trial comparisons
rAAV1-CMV-GAA Administration-cohort 1 vs rAAV1-CMV-GAA Administration-cohort 2: deaths from any cause1 of 30 of 912NCT00976352Trial comparisons
rAAV1-CMV-GAA Administration-cohort 1 vs rAAV1-CMV-GAA Administration-cohort 2: serious adverse events1 of 33 of 912NCT00976352Trial comparisons
Regimen A: Alglucosidase Alfa and Cyclophosphamide vs Regimen B: Alglucosidase Alfa, Rituximab and Methotrexate: deaths from any cause0 of 11 of 34NCT00701701Trial comparisons
Regimen A: Alglucosidase Alfa and Cyclophosphamide vs Regimen B: Alglucosidase Alfa, Rituximab and Methotrexate: serious adverse events1 of 13 of 34NCT00701701Trial comparisons
Alglucosidase Alfa 4000 L Material (Non-US Participants) vs Alglucosidase Alfa 160 L Material (US Participants): Number of Participants With Invasive Ventilator-Free Survival1 of 12 of 34NCT01597596Trial comparisons
Alglucosidase Alfa 4000 L Material (Non-US Participants) vs Alglucosidase Alfa 160 L Material (US Participants): serious adverse events0 of 13 of 34NCT01597596Trial comparisons

diseases-2026-09-18-0.1.0

Sources 6

  • ClinicalTrials.gov's posted results, through CTTI's AACTFreely available. Acknowledgement requested
  • ChEMBL, through Open TargetsCC BY-SA 3.0
  • ClinicalTrials.govNo license stated
  • NLM's MeSHNLM's terms
  • Open TargetsCC0 1.0
  • PubMedNLM's terms
Each source's terms
  • ClinicalTrials.gov's posted results, through CTTI's AACTClinicalTrials.gov data via Aggregate Analysis of ClinicalTrials.gov (AACT), CTTI. CTTI makes its materials freely available and requests acknowledgement. https://aact.ctti-clinicaltrials.org/documentation/299
  • ChEMBL, through Open TargetsCC BY-SA 3.0, for the parts from ChEMBL. Read on 8 Nov 2026 at https://platform-docs.opentargets.org/licence
  • ClinicalTrials.govnone stated
  • NLM's MeSHNLM's
  • Open TargetsCC0 1.0. Open Targets asks that users cite its latest paper: Buniello et al. 2025, Open Targets Platform: facilitating therapeutic hypotheses building in drug discovery, Nucleic Acids Research 53(D1):D1467, PMID 39657122. Read on 8 Nov 2026 at https://platform-docs.opentargets.org/licence
  • PubMedNLM's terms

ClinicalTrials.gov's data carry an international copyright outside the United States: https://clinicaltrials.gov/about-site/terms-conditions.

For software

Read this list from software.

Twenty rows a page, as JSON. No key.

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