Disease · MONDO_0010200
Trials20
Trials an Open Targets clinical report links to the disease, posted results first, then the largest. A trial is shown when the release's checks confirm its link to the disease and Drugs and targets shows its link to one of the disease's drugs.
1 to 20 of 20
Download this page as JSON| Trial | Title | Phase | Participants | Results first posted | Conditions | Drugs | Linked by | Source |
|---|---|---|---|---|---|---|---|---|
| NCT03403205 | Efficacy and Safety of ALXN1840 Administered for 48 Weeks Versus Standard of Care in Participants With Wilson Disease | Phase 3 | 214 | 2023-10-10 | Wilson Disease | TIOMOLIBDATE CHOLINE | Its record names the disease | ClinicalTrials.gov |
| NCT03539952 | Trientine Tetrahydrochloride (TETA 4HCL) for the Treatment of Wilson's Disease | Phase 3 | 77 | 2023-04-20 | Wilson Disease | TRIENTINE TETRAHYDROCHLORIDE | Its record names the disease | ClinicalTrials.gov |
| NCT02763215 | The Assessment of Copper Parameters in Wilson Disease Participants on Standard of Care Treatment | 64 | 2020-10-26 | Wilson Disease | COPPER, PENICILLAMINE, TRIENTINE | Its record names the disease | ClinicalTrials.gov | |
| NCT05047523 | Study of ALXN1840 Versus Standard of Care in Pediatric Participants With Wilson Disease | Phase 3 | 40 | 2024-10-15 | Wilson Disease | TIOMOLIBDATE CHOLINE | Its record names the disease | ClinicalTrials.gov |
| NCT00212355 | Efficacy and Safety, Long-term Study of Zinc Acetate to Treat Wilson's Disease in Japan. | Phase 3 | 37 | 2014-05-14 | Wilson's Disease | ZINC ACETATE | Its record names the disease | ClinicalTrials.gov |
| NCT04422431 | Copper Concentration & Histopathologic Changes in Liver Biopsy in Participants With Wilson Disease Treated With ALXN1840 | Phase 2 | 31 | 2023-07-03 | Wilson Disease | TIOMOLIBDATE CHOLINE | Its record names the disease | ClinicalTrials.gov |
| NCT02273596 | Efficacy and Safety Study of WTX101 (ALXN1840) in Adult Wilson Disease Patients | Phase 2 | 29 | 2021-09-29 | Wilson Disease | TIOMOLIBDATE CHOLINE | Its record names the disease | ClinicalTrials.gov |
| NCT04573309 | Copper and Molybdenum Balance in Participants With Wilson Disease Treated With ALXN1840 | Phase 2 | 9 | 2023-10-27 | Wilson Disease | TIOMOLIBDATE CHOLINE | Its record names the disease | ClinicalTrials.gov |
| NCT01472874 | Single Daily Dosage of Trientine for Maintenance Treatment for Wilson Disease | Not applicable | 8 | 2014-05-19 | Wilson Disease | TRIENTINE | Its record names the disease | ClinicalTrials.gov |
| NCT03957720 | The Individual Therapy for Patients With Wilson's Disease | Early phase 1 | 400 | Wilson's Disease | PENICILLAMINE, ZINC GLUCONATE | Its record names the disease | ClinicalTrials.gov | |
| NCT00004339 | Study of Tetrathiomolybdate in Patients With Wilson Disease | Phase 3 | 90 | Wilson Disease | TRIENTINE | Its record names the disease | ClinicalTrials.gov | |
| NCT02426905 | Study to Assess Long-Term Outcomes of Trientine in Wilson Disease Patients Withdrawn From Therapy With d-Penicillamine | Phase 4 | 90 | Wilson Disease | TRIENTINE | Its record names the disease | ClinicalTrials.gov | |
| NCT04884815 | A Phase 1/2/3 Study of UX701 Gene Therapy in Adults With Wilson Disease | Phase 1/2 | 82 | Wilson Disease | RIVUNATPAGENE MIZIPARVOVEC | Its record names the disease | ClinicalTrials.gov | |
| NCT06762509 | The Clinical Study of Botulinum Toxin Type A Injection in the Treatment of Wilson Disease | 60 | Wilson Disease | BOTULINUM TOXIN TYPE A | Its record names the disease | ClinicalTrials.gov | ||
| NCT03299829 | A Retrospective Study to Assess the Clinical Efficacy and Safety of Trientine in Wilson's Disease Patients | 48 | Trientine Treatment for Wilson's Disease | TRIENTINE | Its record names the disease | ClinicalTrials.gov | ||
| NCT07465718 | Trientine Tetrahydrochloride Administered Once a Day for the First Line Treatment of Wilson's Disease Patients. | Phase 3 | 38 | Wilson's Disease | PENICILLAMINE, TRIENTINE TETRAHYDROCHLORIDE | Its record names the disease | ClinicalTrials.gov | |
| NCT01874028 | A Phase 1 Study to Assess the Effects in the Body of a Single Dose of Trientine Dihydrochloride in Wilson's Disease Patients | Phase 1 | 20 | Wilson's Disease | TRIENTINE | Its record names the disease | ClinicalTrials.gov | |
| NCT07010575 | Patient Preference Study: Standard of Care Versus Once-daily Trientine Tetrahydrochloride | Phase 2 | 10 | Wilson's Disease | TRIENTINE | Its record names the disease | ClinicalTrials.gov | |
| NCT00212368 | Efficacy and Safety Study of Zinc Acetate to Treat Wilson's Disease in Japan. | Phase 3 | Wison's Disease | ZINC ACETATE ANHYDROUS | Its record names the disease | ClinicalTrials.gov | ||
| NCT05686564 | Early Access Program for ALXN1840 in Patients With Wilson Disease | Wilson Disease | TIOMOLIBDATE CHOLINE | Its record names the disease | ClinicalTrials.gov |
diseases-2026-09-18-0.1.0
Sources 6
- ClinicalTrials.gov's posted results, through CTTI's AACTFreely available. Acknowledgement requested
- ChEMBL, through Open TargetsCC BY-SA 3.0
- ClinicalTrials.govNo license stated
- NLM's MeSHNLM's terms
- Open TargetsCC0 1.0
- PubMedNLM's terms
Each source's terms
- ClinicalTrials.gov's posted results, through CTTI's AACTClinicalTrials.gov data via Aggregate Analysis of ClinicalTrials.gov (AACT), CTTI. CTTI makes its materials freely available and requests acknowledgement. https://aact.ctti-clinicaltrials.org/documentation/299
- ChEMBL, through Open TargetsCC BY-SA 3.0, for the parts from ChEMBL. Read on 8 Nov 2026 at https://platform-docs.opentargets.org/licence
- ClinicalTrials.govnone stated
- NLM's MeSHNLM's
- Open TargetsCC0 1.0. Open Targets asks that users cite its latest paper: Buniello et al. 2025, Open Targets Platform: facilitating therapeutic hypotheses building in drug discovery, Nucleic Acids Research 53(D1):D1467, PMID 39657122. Read on 8 Nov 2026 at https://platform-docs.opentargets.org/licence
- PubMedNLM's terms
ClinicalTrials.gov's data carry an international copyright outside the United States: https://clinicaltrials.gov/about-site/terms-conditions.
For software
Read this list from software.
Twenty rows a page, as JSON. No key.
GET https://conductscience.org/api/diseases/v1/MONDO_0010200/trials